Scientific Research Grants

Creation of plasmid and efficacy study for MPS IIIC clinical trial

Cure Sanfilippo Foundation has funded New York-based Phoenix Nest, Inc. The funding supports creation of plasmid and the required in-vivo efficacy study in the Sanfilippo Type C (MPS IIIC) mouse model. These and other steps will enable the project to be evaluated by...

Re-Purposing FDA-Approved Inflammation Drug for Sanfilippo

Cure Sanfilippo Foundation is sponsoring an “Open-label Study of Anakinra in MPS III” clinical trial in collaboration with The Lundquist Institute (formerly LABiomed), and Sobi (Swedish Oprhan Biovitrium AB). This study is an open-label, single-arm, no placebo or...