Therapeutic Avenues Being Investigated
What avenues for treating or curing Sanfilippo Syndrome are being explored by scientists?
Current Clinical Trials
See all the clinical trials underway for Sanfilippo Syndrome.
Research Funded by Cure Sanfilippo
These are some of the most-recent scientific projects, including clinical trials, funded by Cure Sanfilippo Foundation.
Cure Sanfilippo Foundation is sponsoring an “Open-label Study of Anakinra in MPS III” clinical trial in collaboration with The Lundquist Institute (formerly LABiomed), and Sobi (Swedish Oprhan Biovitrium AB).This study is an open-label, single-arm, no placebo or...
Cure Sanfilippo Foundation has again collaborated with Sanfilippo Children's Foundation of Australia to fund a new research project by TIGEM, investigating new therapeutic strategies for the treatment of the behavioral symptoms of Sanfilippo Syndrome (MPS III).TIGEM...
Cure Sanfilippo Foundation is excited to grant funding to LA BioMed for the advancement of Dr. Michelina Iacovino’s work in the field of regenerative medicine for the treatment of Sanfilippo Syndrome (MPS III). This innovative work will utilize CRISPR gene editing to...
Cure Sanfilippo Foundation is pleased to support the work of Dr. Jan Nolta’s lab in collaboration with biotech partner Neuralstem. This project aims to develop an off-the-shelf neural stem cell therapy for patients with Sanfilippo Syndrome (MPS IIIA).As the Director...
Cure Sanfilippo Foundation is funding new research to develop nematode and fly disease models and screening compounds for Sanfilippo Syndrome Type A (MPS IIIA) and Type B (MPS IIIB).
Learn more about all of the research funded by the Foundation, as well the thought-leadership projects the Foundation supports, on the “What We Do” page.
Research & Science News
Find out the latest news regarding research on Sanfilippo Syndrome.