Current Research on Sanfilippo

Therapeutic Avenues Being Investigated

What avenues for treating or curing Sanfilippo Syndrome are being explored by scientists?

Current Clinical Trials

See all the clinical trials underway for Sanfilippo Syndrome.

Research Funded by Cure Sanfilippo

These are some of the most-recent scientific projects, including clinical trials, funded by Cure Sanfilippo Foundation.

Antifungal immunity in patients with mucopolysaccharidosis (MPS)

Cure Sanfilippo Foundation is funding the first year of a two-year study of antifungal immunity in patients with mucopolysaccharidosis (MPS) by investigator Neta Shelzinger, PhD, at Koret School of Veterinary Medicine  in collaboration with Sheba Institute for Rare...

Re-Purposing FDA-Approved Inflammation Drug for Sanfilippo

Cure Sanfilippo Foundation is sponsoring an “Open-label Study of Anakinra in MPS III” clinical trial in collaboration with The Lundquist Institute (formerly LABiomed), and Sobi (Swedish Oprhan Biovitrium AB).This study is an open-label, single-arm, no placebo or...

Learn more about all of the research funded by the Foundation, as well the thought-leadership projects the Foundation supports, on the “What We Do” page.

Research & Science News

Find out the latest news regarding research on Sanfilippo Syndrome.