Tackling Sanfilippo Syndrome From All Angles
Your support funds extensive research into multiple avenues for a treatment/cure, as well as spearheads, supports, and funds initiatives that create valuable disease-specific and patient-preference information about Sanfilippo. All of which leads to more effective treatments, and opportunities for earlier diagnosis.
Your support has enabled Cure Sanfilippo Foundation to commit more than $8.5 million to fund and/or to architect 30+ scientific research projects and clinical trials, to conduct qualitative research supporting development of patient-centered treatments, and to refine technologies that could lead to earlier diagnoses.
Your Support Drives Projects With Wide-Spread Impact
Progress You Support
It will take a mix of complementary and/or supplementary treatments to truly come to a functional “cure” for Sanfilippo Syndrome. This may be several different treatments over their lifetime. That is the reason we fund the most-promising science in a variety of research areas
Research & Grants
Thanks to your support, Cure Sanfilippo Foundation funds scientific research exploring multiple avenues for a treatment/cure to Sanfilippo Syndrome. Learn more about all of the research supported by Foundation grants.
Curing Sanfilippo Syndrome is our ultimate goal, and your support also allows us to play a critical roll in influencing the road that leads there. Learn more about the Foundation’s thought-leadership projects.
We believe that bringing together and working with the brightest minds in the world will make a treatment and/or cure happen sooner. Learn more about the Foundation’s collaborative mindset.
Poster Presentations & Publications
The sharing of information will accelerate discovery of a cure for Sanfilippo, which is why we share as much information as possible through poster presentations and publications. We also urge the researchers we fund to do the same.
ADVANCE, a Sanfilippo Community Conference, is an annual virtual that brings together families and caregivers, scientists and researchers, clinicians and therapists, advocates, biotechs, and supporters from around the world. All to engage and advance the work to help children with Sanfilippo Syndrome.
Interested in Working Together?
Are you a looking for funding for a project related to Sanfilippo Syndrome? Or interested in getting expert insights into the disease? Learn more.