
We Are Working To Cure Sanfilippo Syndrome.
Our mission is simple:
To advocate for and fund research directed towards a cure and treatment options for patients with Sanfilippo Syndrome.

About the Foundation
Explore how the Foundation began, who leads it, the families that partner with it, and the impact it has had since it was founded.
Accelerate Research
Cure Sanfilippo conducts and funds promising research, projects, and clinical trials. Learn more about our research efforts.
Drive Collaboration
Together, a cure comes sooner. We collaborate with families, researchers, academic institutions, regulators, and bio-technology companies.
Increase Awareness
The more people who know about Sanfilippo, the more progress that happens to find a cure. So we help elevate awareness of Sanfilippo.
Raise Funds
We set ambitious annual fundraising goals in order to fund research for every kind of Sanfilippo and to dictate and accelerate the pace of research.
Support/Unite Families
Cure Sanfilippo connects families globally with the latest information on current research, as well as provides support for fundraising and caring for their children.
Cure Sanfilippo Foundation is a 501(c)3 Not-For-Profit Organization
All net funding goes to the urgent mission to advance treatment options to treat children with Sanfilippo.
This is led by proactive families of children with Sanfilippo Syndrome and their supporters, who work tirelessly to change the fate and future for these children.
Donations may be tax-deductible.
Latest Foundation News
Researchers publish results of previously-terminated Sanfilippo Type A enzyme replacement study
Study results from Sobi's previously-terminated Sanfilippo Type A enzyme replacement study have been released. The study results were published in the August 2022 edition of Molecular Genetics and Metabolism and provide some important insights. For context, this...
Sanfilippo research funding available from Foundation
Cure Sanfilippo Foundation now have three funding opportunities available for innovative research into Sanfilippo syndrome (MPS III). Cure Sanfilippo Foundation seeks to support research that fills critical gaps in current knowledge across basic science, clinical...
Replay of ADVANCE 2022, Sanfilippo conference, available on-demand
The virtual ADVANCE 2022, Sanfilippo Community Conference, July 7-8, 2022, brought together families and caregivers, scientists and researchers, clinicians and therapists, advocates, biotechs, and supporters. All to engage and advance the work to help children...
Registration is open for ADVANCE 2022: Sanfilippo Community Conference
Registration is open for ADVANCE 2022: Sanfilippo Community Conference! A virtual conference on July 7-8, bringing together families and caregivers, scientists and researchers, clinicians and therapists, advocates, biotechs, and supporters. All to engage and advance...
Recent scientific articles relevant to Sanfilippo Syndrome: June 9, 2022, digest
Every week thousands of scientific articles on various topics are published. Here are some recent articles and abstracts that are relevant to understanding, managing, and/or treating Sanfilippo Syndrome (mucopolysaccharidosis III or MPS III)."The Inflammation in the...
Upcoming Events
2022 Saving Rylan Golf Tournament | Aug. 21, 2022 – Crossville, TN
Support research to cure Sanfilippo Syndrome by joining the 7th annual Saving Rylan Golf Tournament on Sunday, Aug. 21, 2022, at Bear Trace Golf Course. The 2022 Saving Rylan Golf Tournament honors Rylan Hyder, who lives in Crossville and has Sanfilippo Syndrome....
2022 Tee Off Fore A Cure | Aug. 27, 2022 – New Berlin, WI
Enjoy a day of fun at the seventh annual Levi's Life, Love & Laughter "Tee Of For A Cure" golf tournament on Aug. 27, 2022, at the New Berlin Hills Golf Course. The day's format is a foursome scramble where each team plays the best ball of the foursome for a total...
2022 Bay City Masonic Car Show | Aug. 27, 2022 – Bay City, MI
Check out fantastic cars while also helping fund research for children with Sanfilippo Syndrome at the 2022 Bay City Masonic Car Show on Aug. 27.The 2022 Bay City Masonic Car Show will take place in the Bay City Scottish Rite Masonic Center Parking Lot (614 Center...
MickeyFest 2022! | Sept. 17, 2022 – Delaware City, DE
Join the Delaware City community for another FREE, family-friendly, musical spectacular MickeyFest 2022! All to help Mickey and other children with Sanfilippo Syndrome.MickeyFest 2022! will be celebrated at the Fort DuPont Preservation Lands in Delaware City, DE. This...
Giving Tuesday 2022 | Nov. 29, 2022 – Global
Everyone is vying to be the organization you might support on #GivingTuesday2020, thisglobal “day of giving.” We’ll be honest; we aren’t any different. And because we're rare, every donor and dollar matters. We’re hoping you’ll donate to Cure Sanfilippo Foundation...