What is Happening In Sanfilippo Research?
Stay up to date on the latest information regarding scientific aspects of Sanfilippo Syndrome and progress to find a treatment or cure.
Recent News
JR-441 Enzyme Replacement | Type IIIA | Phase I-II | JCR
Page last updated: October 23, 2023 For web accessibility options: Click/tap the floating blue icon on the right. Trial Information Phase I/II Study of JR-441 in Patients With Mucopolysaccharidosis Type IIIA A Phase I/ II, open-label, randomized, 2-arm study,...
$8 million awarded to study brain cell death in fatal pediatric diseases, including Sanfilippo
Washington University School of Medicine (St. Louis, MO) has received nearly $8 million from the National Institute of Neurological Disorders and Stroke of the National Institutes of Health (NIH) to help determine the root causes of brain cell death in fatal pediatric...
Recent scientific articles relevant to Sanfilippo Syndrome: June – July 2023, digest
Every week thousands of scientific articles on various topics are published. Here are some recent articles and abstracts that are relevant to understanding, managing, and/or treating Sanfilippo Syndrome (mucopolysaccharidosis III or MPS III) from June 2023 to July...
Recent scientific articles relevant to Sanfilippo Syndrome: April – May 2023, digest
Every week thousands of scientific articles on various topics are published. Here are some recent articles and abstracts that are relevant to understanding, managing, and/or treating Sanfilippo Syndrome (mucopolysaccharidosis III or MPS III) from April 2023 to May...
Recent scientific articles relevant to Sanfilippo Syndrome: January – March 2023, digest
Every week thousands of scientific articles on various topics are published. Here are some recent articles and abstracts that are relevant to understanding, managing, and/or treating Sanfilippo Syndrome (mucopolysaccharidosis III or MPS III) from January 2023 to March...
Jessica Haywood joins Cure Sanfilippo Foundation board
Jessica Haywood has joined the board for Cure Sanfilippo Foundation, bringing additional data analytics and social media expertise, strategic thinking, and the patient voice and lived experience of life with Sanfilippo Syndrome from a close relative’s perspective. “We...
Other Sources of News
ClinicalTrials.gov
Immediately see when clinical trials for Sanfilippo Syndrome are listed and detailed information.
Sanfilippo News
A site that aggregates news about Sanfilippo Syndrome into a single location.
RARE Cast – Global Genes’ Podcast
Hosted by award-winning journalist Daniel Levine, RARE Cast focuses on the intersection of rare disease with business, science, and policy in a weekly podcast.