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Latest News & Information for Parents

News and information on issues relevant to you as a parent, caregiver, and advocate of a child with Sanfilippo Syndrome.

News From the Foundation

Cure Sanfilippo agrees: The need to use surrogate biomarkers in an accelerated drug approval pathway for diseases like Sanfilippo

A powerful article from Dr. Emil D. Kakkis outlines the critical need for use of surrogate biomarkers in an accelerated drug approval pathway for diseases like Sanfilippo syndrome. In the article, "Aduhelm’s accelerated approval offers a promising roadmap for rare...

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Other Sources of News

SanflippoNews.com