Parent News

Special Books by Special Kids features another Sanfilippo family

Special Books by Special Kids (SBSK) is a nonprofit created by a former teacher of students with special needs who uses interviews to create a more inclusive world. "SBSK started when I was a teacher for students with disabilities. Originally intended to be a book...

10 years ago, we never could have imagined …

This month celebrates 10 years since we established Cure Sanfilippo Foundation, after our daughter Eliza was diagnosed with Sanfilippo Syndrome. Ten years ... it’s hard to believe. At this milestone, it felt natural to celebrate the progress you’ve enabled. And to...

JR-441 Enzyme Replacement | Type IIIA | Phase I-II | JCR

Page last updated: October 23, 2023 For web accessibility options: Click/tap the floating blue icon on the right. Trial Information Phase I/​II Study of JR-441 in Patients With Mucopolysaccharidosis Type IIIA A Phase I/ II, open-label, randomized, 2-arm study,...