Parent News

Special Books by Special Kids features another Sanfilippo family

Special Books by Special Kids (SBSK) is a nonprofit created by a former teacher of students with special needs who uses interviews to create a more inclusive world. "SBSK started when I was a teacher for students with disabilities. Originally intended to be a book...

10 years ago, we never could have imagined …

This month celebrates 10 years since we established Cure Sanfilippo Foundation, after our daughter Eliza was diagnosed with Sanfilippo Syndrome. Ten years ... it’s hard to believe. At this milestone, it felt natural to celebrate the progress you’ve enabled. And to...

JR-441 Enzyme Replacement | MPS IIIA | Phase I-II | JCR

Page last updated: October 23, 2023 For web accessibility options: Click/tap the floating blue icon on the right. Trial Information Phase I/​II Study of JR-441 in Patients With Mucopolysaccharidosis Type IIIA A Phase I/ II, open-label, randomized, 2-arm study,...

Families & friends fighting to ensure Sanfilippo research continues

We are so thankful for the many families who continue hosting events and fundraisers to support critical research -- especially early, novel and translational research -- that the Foundation funds, in addition to clinical trials. Here are several fundraisers that have...

Family Friday 2023: The Hooks Family

Hear directly from the Hooks family – Parents Cory and Jamie, Trenton (age 17, Type A), and siblings Treyven and Tyson!Awareness is a huge part of fighting Sanfilippo Syndrome. With awareness comes caring and understanding, which can lead to support and donations for...