Press Release

Recognizing MPS Awareness Day 2023

Today, May 15, is MPS (Mucopolysaccharidosis) Awareness Day. Sanfilippo Syndrome's official name is Mucopolysaccharidosis Type 3, or MPSIII. Sanfilippo is part of a group of lysosomal storage disorders known as mucopolysaccharidoses or MPS. The other related disorders...

Family Friday 2023: The Esposito Family

Hear directly from the Esposito family – Dave, Elise, Keira, and Keaton!Awareness is a huge part of fighting Sanfilippo Syndrome. With awareness comes caring and understanding, which can lead to support and donations for research that can give children with Sanfilippo...

Family Friday 2023: The Laughlin Family

Hear directly from the Laughlin family – Shea, Erin, and Spencer!Awareness is a huge part of fighting Sanfilippo Syndrome. With awareness comes caring and understanding, which can lead to support and donations for research that can give children with Sanfilippo more...

U.S. patients: Denali’s natural history study still enrolling

Reminder: Denali Therapeutics is still enrolling patients with Sanfilippo Syndrome Type IIIA for its two-year natural history study. Denali Therapeutics is developing an enzyme replacement therapy for individuals with Sanfilippo type A. As part of their development...

Family Friday 2023: The Ulrich Family

Hear directly from the Ulrich family – Jericho, Christin, Elise, and Veda!Awareness is a huge part of fighting Sanfilippo Syndrome. With awareness comes caring and understanding, which can lead to support and donations for research that can give children with...