Scientific News

Foundation crosses $1 million mark in 2020 fundraising

Cure Sanfilippo Foundation supporters have raised more than $1 million in 2020 so far, to fund research into Sanfilippo Syndrome! "When the World shut down in March, we knew we couldn't stop the time-sensitive mission to help children. But we didn't know what the...

Global Genes’ RARE Cast podcast interviews Cara O’Neill

Dr. Cara O'Neill, Chief Science Officer for Cure Sanfilippo Foundation, discussed her own journey with Sanfilippo Syndrome, issues causing diagnostic delay, and how the Foundation is helping advance science for a cure in an interview as the Aug. 28 guest on Global...

VIDEO: What Craig & Sara want to say to you

https://youtu.be/dOxewsJad4w This is Craig and Sara. Their beautiful son Carson is participating in a new clinical trial that your generosity made happen. This is their message to you. Your support enabled Cure Sanfilippo Foundation to build this clinical trial...

Key Points of Sanfilippo Advocacy Group Response to FDA Guidance

The combined Sanfilippo Advocacy group submitted comments to the U.S. Food and Drug Administration's (FDA) on May 5, 2020, regarding its draft guidance on drug development for Sanfilippo Syndrome for review.  These advocacy group is working closely with the FDA on the...