Washington University School of Medicine (St. Louis, MO) has received nearly $8 million from the National Institute of Neurological Disorders and Stroke of the National Institutes of Health (NIH) to help determine the root causes of brain cell death in fatal pediatric...
Scientific News
Recent scientific articles relevant to Sanfilippo Syndrome: June – July 2023, digest
Every week thousands of scientific articles on various topics are published. Here are some recent articles and abstracts that are relevant to understanding, managing, and/or treating Sanfilippo Syndrome (mucopolysaccharidosis III or MPS III) from June 2023 to July...
Recent scientific articles relevant to Sanfilippo Syndrome: April – May 2023, digest
Every week thousands of scientific articles on various topics are published. Here are some recent articles and abstracts that are relevant to understanding, managing, and/or treating Sanfilippo Syndrome (mucopolysaccharidosis III or MPS III) from April 2023 to May...
Recent scientific articles relevant to Sanfilippo Syndrome: January – March 2023, digest
Every week thousands of scientific articles on various topics are published. Here are some recent articles and abstracts that are relevant to understanding, managing, and/or treating Sanfilippo Syndrome (mucopolysaccharidosis III or MPS III) from January 2023 to March...
Jessica Haywood joins Cure Sanfilippo Foundation board
Jessica Haywood has joined the board for Cure Sanfilippo Foundation, bringing additional data analytics and social media expertise, strategic thinking, and the patient voice and lived experience of life with Sanfilippo Syndrome from a close relative’s perspective. “We...
Sanfilippo researchers, leaders discuss data sharing to advance Sanfilippo Syndrome therapeutic development
Meeting summary now available to download Sanfilippo syndrome is an ultra-rare, neurometabolic disease which leads to severe neurodegeneration and multisystemic impacts for those affected. Individual heterogeneity, the protracted timespan of disease evolution across...
Packed days for Foundation leaders attending WORLDSymposium 2023, including presenting
Page reviewed by:Â Dr. Cara O'Neill, FAAPPage last updated:Â March 14, 2023For web accessibility options: Click/tap the floating blue icon on the right. Leaders of Cure Sanfilippo Foundation were once again busy during WORLDSymposium 2023. The six-day international...
Recent scientific articles relevant to Sanfilippo Syndrome: October-December 2022, digest
Every week thousands of scientific articles on various topics are published. Here are some recent articles and abstracts that are relevant to understanding, managing, and/or treating Sanfilippo Syndrome (mucopolysaccharidosis III or MPS III) from October 2022 to...
Podcast Episode 12: New Sanfilippo drug repurposing clinical trial; updates on other research + more
The Foundation's "A Close Look at Sanfilippo" podcast spends 10 minutes diving into five hot topics regarding Sanfilippo Syndrome, a rapidly degenerative disease in children currently with no FDA-approved treatment. In podcast episode 12, president and co-founder of...