Every parent dreams about their kid’s future and watching it unfold.
Sanfilippo Syndrome takes all that away, replacing it with pain and suffering. The child experiences severe dementia and dies in their mid-teens. All before their parents eyes.
Cure Sanfilippo Foundation architects and funds cutting-edge research to accelerate discovery of a treatment or cure for Sanfilippo Syndrome so parents can dream of their children’s futures again.
$12.5 million raised since 2013 15,000 children globally 35+ research projects funded 100+ partner families globally 3 clinical trials funded Medical & scientific expertise
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Every parent dreams about their child’s future and watching it unfold.
Sanfilippo Syndrome takes that all away.
Help save children
$12.5 million raised since 2013
Medical & scientific expertise
35+ research projects funded
Multiple clinical trials fundedDONATE
FUNDRAISE
TELL OTHERS
DONATE
FUNDRAISE
TELL OTHERS
By advocating for and funding research directed towards a cure and treatment options.
The Foundation’s focus in 2022: funding the most-promising research and elevating the voices of caregivers in pursuit of a cure for Sanfilippo syndrome.
Fundraising is critical fuel for these goals. Our goal is to raise $2,000,000 in 2022. We need your help to get there. Every single donation makes a difference.
Sanfilippo parents unite on TikTok to raise $1M in 1 month for research for the deadly childhood disease
TikTok community donates more than $20,000 in 24 hours to support Sanfilippo research Several families of children with Sanfilippo Syndrome have been spreading awareness by sharing their journey with the disease and have amassed significant followings on TikTok over...
Natural History of Biomarkers & Clinical Outcomes | Type IIIA | Observational Study | Denali
Trial Information Denali Therapeutics is conducting a observational research study, which can also be called a natural history study, into Sanfilippo syndrome Type A (MPS IIIA). The purpose of the research study is to collect blood and behavioral information from...
Denali sponsoring observational research study (natural history) for Sanfilippo Type A
Denali Therapeutics has provided information about their observational research study natural history) for children with Sanfilippo Syndrome Type A. Below is a flyer provided by Denali. More information and sign-up is available here.From the study website, the purpose...
@curesanfilippo I believe. In honor of my daughter Eliza & all children with Sanfilippo ❤ #tiktokforacure #workyourmagic #curesanfilippo ♬ original sound - curesanfilippo