Page last updated: May 14, 2026 For web accessibility options: Click/tap the floating blue icon on the right.Study Summary In this multi-center, natural history study of subjects with Sanfilippo syndrome type C (MPS IIIC), patients will be monitored over a 2-year...
Observational Study
A Natural History Study of Patients With Sanfilippo Disease(s) (MPS3) | MPS IIIA, IIIB, IIIC, IIID | Observational Study | Lysosomal Center
Page last updated: January 31, 2023 For web accessibility options: Click/tap the floating blue icon on the right.Trial Information Lysosomal and Rare Disorders Research and Treatment Center, Inc. is conducting a natural history study of patients with Sanfilippo...