Historical-Trial

LYS-SAF302 Gene Therapy | MPS IIIA | Phase II-III | Lysogene

Page last updated: February 19, 2024 Page reviewed by: Dr. Cara O'Neill, FAAP For web accessibility options: Click/tap the floating blue icon on the right.Summary Study: “Open-label, Single-arm, Multi-center Study of Intracerebral Administration of Adeno-associated...