Update: April 2021 This Phase 1/2 trial has now fully enrolled and is not accepting additional patients.We are hopeful that a Phase 3 trial will be initiated in the future but no timeline is currently available.Trial Information EGT-101 is Esteve's potential...
Gene Therapy
SNG-101 Gene Therapy | MPS IIIB | Phase I-II | Sangrail
Page last updated: May 5, 2026 Page reviewed by: Dr. Cara O'Neill, FAAP For web accessibility options: Click/tap the floating blue icon on the right.Summary Information The SNG-101 (formerly ABO-101) gene therapy uses an adeno-associated virus serotype 9 carrying the...