Page last updated: May 5, 2026 Page reviewed by: Dr. Cara O'Neill, FAAP For web accessibility options: Click/tap the floating blue icon on the right.Summary Information The SNG-101 (formerly ABO-101) gene therapy uses an adeno-associated virus serotype 9 carrying the...
Gene Therapy
UX111 Gene Therapy | MPS IIIA | Phase I-II-III | Ultragenyx
Page last updated: July 17, 2026 Page reviewed by: Dr. Cara O'Neill, FAAP For web accessibility options: Click/tap the floating blue icon on the right.Summary Information The UX111 (formerly ABO-102) Gene Therapy uses a self-complementary adeno-associated virus...