At this milestone, it felt natural to celebrate the progress you’ve enabled. And to also keep the ultimate goal in sight: effective and available treatments for all children with Sanfilippo Syndrome. For every child. For every type of Sanfilippo.
And while we aren’t there yet, you help us move closer every day. You’ve enabled significant progress to happen in pursuit of that ultimate goal.
The following look backs at the tremendous progress and activity that your generous support made possible. And charts what is on the horizon.
The reality is that this work has happened for one reason, and one reason only: you.
On a personal note, it has been incredibly difficult to see the day-to-day progression of the disease in our daughter Eliza, but we celebrate all she can do. Sometimes it might just be a glimmer in her eyes that lets us know she’s happy or enjoying something. We love her with all of our heart.
We are forever grateful for you and your kind support. You are bringing HOPE to so many families. Thank you!
– Glenn and Cara O’Neill, Co-Founders and Parents of Eliza