This is Craig and Sara. Their beautiful son Carson is participating in a new clinical trial that your generosity made happen. This is their message to you.
Your support enabled Cure Sanfilippo Foundation to build this clinical trial with The Lundquist Institute that is giving Carson and other children an FDA-approved medication, Anakinra, to reduce a body-wide inflammation caused by Sanfilippo Syndrome.
This trial could establish the first-ever treatment for Sanfilippo Syndrome and provide all children with relief from disease-related symptoms. And it’s happening, even amidst a pandemic, because of your generosity and commitment.
Click here to continue supporting efforts like there to bring treatments to children.