The following letter was released by Sobi on June 24, 2019, regarding its enzyme-replacement therapy clinical trial for Type A.
JR-441 Enzyme Replacement | Type IIIA | Phase I-II | JCR
Page last updated: October 23, 2023 For web accessibility options: Click/tap the floating blue icon on the right. Trial Information Phase I/II Study of JR-441 in Patients With Mucopolysaccharidosis Type IIIA A Phase I/ II, open-label, randomized, 2-arm study,...