When children with a rare disease are diagnosed at birth, they have the greatest opportunity to receive timely, approved treatments or participate in clinical trials that can provide them better quality of life and less pain and suffering. Early diagnosis and...
Funding Development of Nematode & Fly Disease Models and Screening Compounds
September 6, 2018
Cure Sanfilippo Foundation is funding new research to develop nematode and fly disease models and screening compounds for Sanfilippo Syndrome Type A (MPS IIIA) and Type B (MPS IIIB).