Cure Sanfilippo Foundation is funding new research to develop nematode and fly disease models and screening compounds for Sanfilippo Syndrome Type A (MPS IIIA) and Type B (MPS IIIB).
Blood-based biomarkers for Sanfilippo syndrome progression and treatment
Grant Summary Institution: University of California, Los Angeles Primary Investigator: Gal Bitan, Ph.D./Professor of Neurology Duration: 24 months Start Date: September 2021 Type of Sanfilippo studied: Types A, B, C, and D Types of Sanfilippo that could benefit: Types...